患有这种疾病的人只缺少一种基因,这种基因把光转化成信号并传入大脑,然后使眼睛发挥作用。
The hope is that adding that gene through a one-time CRISPR treatment will cure them, permanently editing their DNA and letting them see.
希望通过一次CRISPR治疗就可以植入这种基因,并治愈这种疾病,使DNA被永久性编辑,让他们得见光明。
This is undoubtedly a more noble use of CRISPR than making spicy tomatoes.
比起制造辣味的西红柿,这无疑是CRISPR技术的一项更崇高的运用。
It's a good trial for the cutting-edge—and controversial—technology, because there's already some solid proof that the disease is treatable on a genetic level.
对于这项先进且有争议的技术而言,这是一次不错的尝试,因为已有可靠的证据表明这种疾病在基因层面上是可治疗的。
Thanks to a gene therapy called Luxturna, which is already on the market, scientists know that injecting a replacement gene into cells in the retina can cure the ailment .
多亏已经上市的Luxturna基因疗法,科学家了解到向视网膜中的细胞注入一种替代基因可以治愈疾病。
CRISPR would work by similarly delivering new genetic material to the eye, giving researchers the perfect testing ground for using the new medical procedure in humans, before turning to more complicated diseases like cancer.
【科学家将要用基因编辑技术治疗先天失明】相关文章:
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